Molecular Basis of 1-Deoxygalactonojirimycin Arylthiourea Binding to Human α-Galactosidase A: Pharmacological Chaperoning Efficacy on Fabry Disease Mutants
May 12th, 2014 by Yi Yu, Teresa Mena-Barragán, Katsumi Higaki, Jennifer L. Johnson, Jason E. Drury, Raquel L. Lieberman, Naoe Nakasone, Haruaki Ninomiya, Takahiro Tsukimura, Hitoshi Sakuraba, Yoshiyuki Suzuki, Eiji Nanba, Carmen Ortiz Mellet, José M. García Fernán
ACS Chemical Biology
DOI: 10.1021/cb500143h